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By The Numbers
Gene Therapy
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Expansion
Cognate BioServices and its Gene Therapy Division Cobra Biologics Announce Major Expansion of Manufacturing Facilities in US and Europe
PR-M11-20-034
AAV Platform Technologies
Increasing Predictability with AAV Platform Technologies
PAP-Q4-20-CL-027
Gene Therapy
Anticipating the Next Decade of Gene Therapy
PAO-11-20-CL-02
CRISPR RNPs
CRISPR RNPs and the Future of Cell and Gene Therapy
PAP-Q3-20-CL-002
Cell & Gene Logistics
Standardizing Best Practices for Transporting Cell and Gene Therapies
PAP-Q3-20-CL-013
CRISPR-Cas9
How Close Is CRISPR to Eradicating Disease and Correcting Genetic Defects?
PAP-Q1-20-NI-003
Gene Therapy
Slow Progress and a Shaky Start—What’s Next for Gene Therapy?
PAP-Q4-19-NI-001
Gene Therapy
Introduction: The Promise & Challenge of Gene Therapy
PAP-Q4-19-NI-008
Gene Therapy
Gene Therapy R&D Accelerates
PAP-Q4-19-NI-002
Gene Therapy
Overcoming the Manufacturing Roadblock
PAP-Q4-19-NI-003
Gene Therapy
Promise Amid Challenges: Logistics of the Cell and Gene Therapy Supply Chain
PAP-Q4-19-NI-004
CRISPR-Cas9
CRISPR-Cas9 Milestones: The First In Vivo Clinical Trial Is Now Underway
PAP-Q4-19-CL-011
Plasmids
The Pivotal Role of Plasmid DNA
PAP-Q4-19-CL-006
Drug Approval
BioMarin Going for 2020 Approval of its Hemophilia A Gene Therapy
PAO-M08-19-NI-026
Integration
Building Upon an Integrated Biologics Offering
PTV-M08-19-BIO-005
Gene Therapy
Expanding GMP Gene Therapy Manufacturing Capacity
PTV-M08-19-BIO-003
Gene Therapy
Accelerating Innovation for Gene Therapy
PTV-M08-19-BIO-002
Cell and Gene Therapy
Aldevron to Build 14-Acre Gene Therapy Manufacturing Campus
PR-M06-NI-002
Cell and Gene Therapy
Precision BioSciences Aims for Significant Funding Support based on its ARCUS Gene Editing Tech
PAO-M03-19-NI-013
Cell and Gene Therapy
Massachusetts is Looking for Ways to Help Patients Receive Expensive Gene Therapy
PAO-M01-19-NI-022
FDA
FDA Gives Novartis Gene Replacement Therapy Application Priority Review
PAO-M12-18-NI-003
Licensing Agreement
REGENXBIO Announces Exclusive Worldwide License with Ultragenyx for the Treatment of CDKL5 Deficiency Disorder Using NAV Vectors
PR-M10-18-NI-093
Cell and Gene Therapy
Analytical Methodologies Utilized in Therapeutic Viral Vector Manufacturing
PAP-Q3-18-CL-001
Gene Therapy
Understanding the Unique Design and Engineering Needs for Gene Therapy Production
PAP-Q3-18-CL-008
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